BUKAANKA UGU HOREEYA WELIGII BUKAANKA SI UU HELO DAAWAYNTA JINIINKA
SI DEG DEG AH
JUUN 20, 2023
GREEN BAY, WI- Dadka degan Wisconsin waa bukaankii ugu horeeyay abid ee hemophilia B ee hela daawaynta hidda-wadaha ilaa oggolaanshaha FDA.
"Waxaan dareemayaa sharaf inaan noqdo qofka ugu horreeya ee ka qaybqaata daaweyntan ka baxsan tijaabooyinka bukaan-socodka. Aad ayaan ugu faraxsanahay in aan gacan ka geysan doono caddaynta in tani ay tahay ikhtiyaar daawaynta shakhsiyaadka qaba hemophilia B." - Mason Buxton
HEMGENIX (etranacogene dezaparvovec), oo ay soo saartay uniQure Inc. oo ay qaybisay CSL Behring LLC, ayaa FDA ogolaatay Noofembar 2022 waxaana loogu talagalay daawaynta dadka qaangaarka ah ee qaba Hemophilia B (Factor IX Deficiency) kuwaas oo hadda isticmaala Factor IX therapy ka hortagga, ama hadda haysta ama dhiigbax taariikhi ah oo nolosha-halis ku ah, ama soo noqnoqday, dhacdooyin dhiigbax ah oo iskiis ah oo halis ah.
Hemophilia B waa cillad dhiig-bax hidde-side ah oo ka dhalatay heerka xinjirowga dhiigga ee maqan ama aan ku filnayn Qodobka IX, borotiinka loo baahan yahay si loo soo saaro xinjiro dhiig si loo joojiyo dhiigbaxa. Calaamadaha waxaa ka mid noqon kara dhiig-bax dheer ama culus ka dib dhaawac, qaliin, ama habka ilkaha; xaaladaha daran, qaybaha dhiigbaxa waxay ku dhici karaan si kedis ah iyada oo aan sabab cad loo helin. Dhiigbaxa daba dheeraada waxay u horseedi karaan dhibaatooyin halis ah, sida dhiigbaxa kala goysyada, murqaha ama xubnaha gudaha, oo ay ku jirto maskaxda. (Guddiga, O. of the (2022) FDA waxay ansixisay daawaynta hidda-wadaha koowaad si loogu daweeyo dadka waaweyn ee qaba hemophilia B, Maamulka Cuntada iyo Dawooyinka ee Mareykanka. -approves-first-gene-therapy-treat-adults-hemophilia-b#:~:text=Maanta%2C%20the%20U.S.%20Food%20and,current%20or%20historical%20life%2Dthreatening (la galiyay: 23 Laga yaabaa 2023).
In kasta oo HEMGENIX aanu dawo u ahayn bukaanada Hemophilia B, horumarka caafimaadku waxa uu yarayn karaa, haddii kale, baabi'iyo beddelka qodob ka-hortagga toddobaadlaha ah iyo dhiigbaxa.
"HEMGENIX waa qayb muhiim ah oo ku saabsan qaabka daaweynta ee hadda jira iyo horumarinta muddada dheer ee la sugayo ee bulshada hemophilia B," ayuu yiri Matthew Ryan, MD, Dhakhaatiirta Caafimaadka Dadka waaweyn iyo Agaasimaha Caafimaadka ee Xarunta Bixinta Hemophilia, Green Bay, WI. "Daawayntan xiisaha leh waxay siinaysaa bukaanada fursad ay ku noolaadaan nolol aan lahayn dhiig-bax joogto ah ama culeyska faleebo joogto ah. Helitaanka daawayntan cusub ee hal mar ah ayaa sidoo kale dhalinaysa wada-hadallo dheeraad ah oo bulshada dhexdeeda ah marka ay timaaddo ikhtiyaarrada daawaynta iyo yoolalka, taas oo aad muhiim u ah marka la maareynayo xaalad nololeed oo dheer, maadaama baahiyaha shakhsigu ay isbeddeli karaan sababo kala duwan awgood.”
"Aad ayaan ugu faraxsanahay in bukaannadu ay helaan fursadan cusub taas oo u horseedi doonta nolol tayo wanaagsan leh iyo daawaynta kahortaga ah ee hadda! Si ay ugu noolaadaan nolol xor ah oo ka hortag ah oo soo noqnoqota, iyada oo aan walwalkaas ka qabin haddii ay dhiig ku imanayaan ama haddii ay leeyihiin arrimo iyaga la jira, iyaga oo aan ka welwelin waxyeellada ka soo gaarta kala-goysyada dhiigbaxa…. waxay u noqon doontaa iyaga noloshooda. "- Andrea Miller, APNP, Xarunta Wacyigelinta Hemophilia.
